
"They had a 75% disease progression reduction reading and if you hit 75% and above, it's a home run. The data is unequivocal and supports a blockbuster approval scenario for the first ever gene therapy for Huntington's."
The discussion outlines UniQure's (QURE) impressive two-year data readout for their gene therapy targeting Huntington's disease. With a 75% reduction in disease progression, the data exceeded expectations and sets the stage for accelerated FDA approval and robust commercialization potential. This commentary highlights the blockbuster potential of UniQure, emphasizing a significant positive catalyst in a high-stakes biotech environment.
Peter Mantas: uniQure (QURE) and Clearpoint Neuro (CLPT) Inflection
September 26, 2025
Earnings Preview